5 barriers to access for sickle cell disease gene therapies
Sickle cell disease (SCD) is a genetic blood disorder that affects the lives of 100,000 Americans1. SCD causes abnormal hemoglobin molecules in the red blood cells, resulting in cells forming in a crescent or sickle shape, which can block blood vessels and cause pain, organ damage, and other complications. This cellular-level disfunction is addressable with […]