Cardiovascular, Renal, and Hepatic Biomarkers Outside Guideline-Recommended Thresholds: Prevalence and Determinants in Type 1 Diabetes
T1D Exchange published research in Diabetes Technology & Therapeutics using NorstellaLinQ lab data linked to their T1D patient registry and wearable device data. The objective of the study was to evaluate the prevalence of cardiovascular, renal, and hepatic biomarkers that fall outside guideline-based thresholds in adults with type 1 diabetes, and to identify demographic and […]
Rare … but Actually Not That Rare
Rare Disease Day will be commemorated on 28 February this year, as it has been every year since 2008. Coordinated by EURORDIS-Rare Diseases Europe, the day will bring together over 70 national groups across 106 countries in over 600 events to raise awareness and drive policy change for people living with these conditions. Rare diseases are […]
Using Real-World Data to Redefine Evidence for Ultra-Rare Diseases
In ultra-rare diseases, where traditional control arms are often impractical, regulators still require meaningful context to interpret trial outcomes. Here’s how a biotech company leveraged NorstellaLinQ to build a regulatory-grade real-world control dataset that combined deep unstructured clinical notes, AI-enabled data curation, and rigorous propensity score matching. By creating a highly comparable real-world cohort, the […]
NorstellaLinQ: Illuminating the Rare Disease Journey
In rare disease, traditional real-world data sources often fall short, leaving teams across research, medical, and commercial functions with blind spots. But with NorstellaLinQ, biopharma’s first fully integrated data asset, rare disease doesn’t mean unreachable. This infographic explores how NorstellaLinQ lets you: Capture every patient and complete every journey Reveal hidden patients earlier Track real-world […]
Refining Rare Disease Targeting with Real-World Data
A mid-sized pharmaceutical company leveraged NorstellaLinQ to refine rare disease patient targeting with integrated real-world data. By combining EHR physician notes, claims data, and patient journey analysis, the company identified overlooked patient populations, mapped the physicians diagnosing and treating them, and generated actionable insights to improve commercial targeting and early product planning. The company: Learned […]
Uncovering New Rare Disease Patients Using Structured and Unstructured Real-World Data
Learn how integrated structured and unstructured real-world data helped identify rare disease patients, quantify the addressable population, and strengthen commercial and payer strategies ahead of launch. Identified hidden rare disease patients with integrated real-world data Quantified the addressable patient population with confidence Strengthened launch and payer strategies with actionable insights
Breaking Barriers in Rare Disease Drug Development
Bringing rare disease treatments from pipeline to patient Rare diseases affect more than 395 million people worldwide, yet only 5% have an FDA-approved treatment. The challenges of small patient populations, regulatory complexities, and limited clinical data have historically slowed progress. But the landscape is changing. This infographic explores the key barriers in rare disease drug […]
Unlocking Value Potential for a Client’s Rare Disease Treatment
A pharmaceutical manufacturer faced challenges in identifying patients early in the treatment journey for a rare disease, aiming to improve its medication uptake. The client was aiming to: Identify new revenue opportunities by uncovering untreated patient populations Tackle healthcare access disparities affecting underserved groups Optimize provider engagement and reimbursement strategies
A New Era for Patient Recruitment and Retention in Rare Disease
Pharma and biotech organizations continue to prioritize the diversification of their pipelines to innovate more in areas of high and rare unmet need. In addition to delivering life-saving treatments to patients who have had historically limited therapeutic options, addressing high and rare unmet needs can lead to faster routes to market with accelerated regulatory pathways […]
A 26-Year Journey to Reach a Complex Rare Disease Diagnosis
Imagine: it’s Saturday, and you’re at your five-year-old’s soccer game on a beautiful spring day. As she runs down the field, you watch her collapse because her knee just dislocated. This is where Norstella’s Go To Market Director for Patient Engagement & Recruitment, Haley Quinn’s rare disease story starts. At the time of this first […]
